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Tag: MPS

A total of 7 posts are filed under MPS
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UAB Researcher Answered Questions for Families of Children with Rare Diseases
BIRMINGHAM, Alabama – Few people outside his laboratory at the University of Alabama at Birmingham knew or understood what researcher… Continue Reading
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Orphans No More: Renaissance in New Drugs for Rare Diseases
Once famously described as “orphan diseases, too small to be noticed, too small to be funded” in the Hollywood drama Lorenzo’s Oil,… Continue Reading
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Charity Tuesday: Courage to Make a Difference
It’s Charity Tuesday and we want to give a shout-out to a new charity called “Courage to Make a Difference” founded by… Continue Reading
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A RARE DISEASE PATIENT PERSPECTIVE – Roy Zeighami
A Rare Disease Patient Perspective I would like to use this blog post to explain why the rare disease community is different, and why it… Continue Reading
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Genzyme Announces Winners of Patient Advocacy Leadership Award Grants
CAMBRIDGE, Mass., Aug 17, 2011 (BUSINESS WIRE) — Genzyme, a Sanofi company, today announced the first recipients of the Genzyme… Continue Reading
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San Francisco Giants to host Rare Disease Fundraiser for MPS IV – with YouTube sensation Keenan Cahill!
No Question, Brian Wilson and Cody Ross are truly dynamite!!! Check out this article and video and pass it on!… Continue Reading
Former BioMarin exec targets orphan drugs
Emil Kakkis loves orphans. The former chief medical officer at BioMarin Pharmaceutical Inc. — the Novato-based poster child for developing… Continue Reading