There is a tremendous amount of frustration with the current state of rare and orphan drug development. With over 7,000 rare diseases, only 344 therapies & treatments have been developed over 25+ years and the passing of the Orphan Drug Act of 1983.
What have been the road blocks and what is the community currently doing to accelerate drug development.
Here is a  perspective from a rare disease parent advocate on this ongoing debate:
https://addiandcassi.com/wordpress/numbers-dont-add-up-only-344-new-drugs-approved-by-fda-for-30-million-americans-with-rare-disease-in-past-25-years/

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