What if the medication you needed wasn’t available in the United States? Many patients with rare disease face this dilemma. Our newest toolkit, Access to Unapproved Medicine: Is It an Option for Me? (USA), provides information on “Expanded Access” and “Compassionate Use” and the steps one can take to get access to unapproved medicine.
With sections detailing current FDA regulations and other options to obtain access, the toolkit is a comprehensive guide for patients who may currently be, or may one day be, in pursuit of treatment options that are not currently FDA approved.
The toolkit also helps explain the risks of obtaining these sorts of medications, medically, financially, and emotionally.