CureDuchenne, the leading nonprofit focused on finding a cure for Duchenne muscular dystrophy, launched a new website today atwww.CureDuchenne.org to further reflect its mission which focuses on improving and extending the lives of all those with Duchenne.

Duchenne muscular dystrophy is a fatal genetic disorder that causes muscle degeneration and typically effects boys. Currently there are nearly 15,000 boys in the U.S. battling this disease and 300,000 worldwide.  Most boys with Duchenne lose their ability to walk by age 12 and do not survive beyond their mid-20s. As the disease progresses, the simplest of tasks become difficult, and in the later stages, heart and breathing muscles begin to fail. At this time, there is no cure for Duchenne.

“CureDuchenne continues to accelerate the cure, redefine care and build a community for all those impacted by Duchenne,” said Debra Miller, founder and CEO of CureDuchenne. “We are dedicated to finding a cure for this devastating disease. We hope that with the help of the new website, individuals will be able to learn more about Duchenne and take action to help find a cure.”

 

The new website provides resources and information on three core areas:

 

  • Cure:With a goal of finding a cure for all genetic mutations of Duchenne, CureDuchenne is focused on funding the most promising and qualified preclinical and clinical research to save lives. 

 

  • Care:There are limited treatment options for Duchenne patients, and CureDuchenne provides a vital education resource for parents, caregivers and clinicians in order to help ensure loved ones have the best care.

 

  • Community:CureDuchenne brings together families, caregivers and medical professionals to share experiences, advice, and personal stories, giving hope and support to the entire community.

 

The updated website allows viewers to find Duchenne-related resources ranging from research overviews to family stories about those affected with Duchenne. The website also includes information on free upcoming CureDuchenne Cares workshops; clinical trial information; fact sheets and infographics about Duchenne; details on exon skipping; Duchenne care topics such as physical therapy; and more.

The website comes at a pivotal time in continuing CureDuchenne’s progress towards finding a cure. This past year has been a victorious one in many ways, with the approval of the first ever drug to treat Duchenne; though Exondys51 is only effective for 13% of the Duchenne population, it’s a big step in the right direction. Another drug EMFLAZA, a steroid, was also approved for all boys with Duchenne.

CureDuchenne’s research portfolio is also highlighted on the new website in the CureDuchenne Ventures section.  It includes 12 wide-ranging projects to help treat the whole disease.  This pipeline of therapies comes from a diverse array of cutting edge technologies used to treat all aspects of Duchenne.  CureDuchenne Ventures’ early funding helps Duchenne science attract future investments made by venture capital firms, biotech and pharmaceutical companies.     

Learn more at www.CureDuchenne.org. To help save the lives of those with Duchenne, pleasedonate.

 

About CureDuchenne

CureDuchenne was founded in 2003 with a focus on saving the lives of those with Duchenne muscular dystrophy, a disease that affects more than 300,000 boys worldwide. With support from CureDuchenne, nine research projects have advanced to human clinical trials. CureDuchenne also is the innovator bringing physical therapy and standard of care to local communities around the country through CureDuchenne Cares.  For more information, please visit CureDuchenne.org and follow us on FacebookTwitterInstagram and YouTube.

 

 

8 thoughts on “Leader in Cure, Care and Community for Duchenne Muscular Dystrophy CureDuchenne Launches New Website”

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  8. RFID says:

    Would you allow your government to place a microchip in your body?

    Did you know that is the future we are approaching with RFID Microchip technology?

    Even more importantly, did you know there was a man almost 2000 years ago who prophesied of a cashless society in the last days? This mans name is Jesus.

    Did you know that this RFID Microchip matches perfectly with the Mark of the Beast in Revelation 13:16-18?

    “He(the false prophet) causes all, both small and great, rich and poor, free and slave, to receive a mark on their right hand or on their foreheads, and that no one may buy or sell except one who has the mark or the name of the beast, or the number of his name.

    Here is wisdom. Let him who has understanding calculate the number of the beast, for it is the number of a man: His number is 666” (Revelation 13:16-18).

    Referring to the last days, this could only be speaking of a cashless money society, which we have yet to see, but are heading towards. Otherwise we could still buy or sell without the mark among others if physical money was still currency. This mark could not be spiritual, because the word references two distinct physical locations on the body. If it was spiritual, it would just say in the forehead.

    Carl Sanders sat in seventeen New World Order meetings with heads-of-state officials such as Henry Kissinger and Bob Gates of the C.I.A. to discuss plans on how to bring about this one-world system. The government commissioned Mr. Sanders to engineer a microchip for identifying and controlling the peoples of the world-a microchip that could be placed under the skin with a hypodermic needle(a fast, convenient process that would be slowly accepted by society).

    Carl Sanders, along with a team of engineers behind him, with US grant monies provided by tax dollars, took on this challenge and designed a microchip that is powered by a lithium battery, rechargeable through the temperature fluctuations in our skin. Without the knowledge of the Bible(Carl was not a believer at the time), these engineers spent one and a half million dollars doing research on the best and most convenient place to have the microchip placed under the skin.

    These researchers found that the forehead and the back of the hand(the two places Revelation says the mark will go) are not just the most convenient places, but are also the only viable locations for rapid, consistent temperature fluctuations in the skin to recharge the lithium battery. The RFID chip is approximately seven millimeters in length, .75 millimeters in diameter, about the size of a grain of rice. It is capable of storing pages upon pages of information about you. All your general history, work history, crime record, health history, and financial data can be stored on this microchip.

    Brother Sanders believes that this microchip, which he regretfully helped engineer, is the “mark” spoken about in Revelation 13:16-18. The original Greek word for “mark” is “charagma,” which means a “scratch or etching.” It is also interesting to note that the number 666 is a word in the original Greek language. The word is “chi xi stigma,” with the last part, “stigma,” also meaning “to stick or prick. Carl believes this is referring to the use of a hypodermic needle being poked into the human flesh to insert the microchip.”

    Mr. Sanders asked a doctor what would occur if the lithium contained within the RFID microchip leaked into the body. The doctor responded by saying a terrible sore would appear in that spot. This is what the book of Revelation has to say:

    “And the first(Angel) went, and poured out his vial on the earth; and there fell a noisome and grievous sore on the men which had the mark of the beast, and on them which worshipped his image” (Revelation 16:2).

    The Bible tells us we cannot buy or sell without the mark of the beast, or the number of its name. This number is identified as 666. The Bible tells us to calculate the number 666.

    In this world we are identified by numbers, whether it is our social security number, drivers license, or cards used to make payments. The number of the beast represents something like this, to identify us in a one world government system. This number will be contained within the microchip to identify each and every one of us so we may buy or sell.

    To see the hidden meaning behind calculating the number 666(6+6+6=18), and how it matches up with scipture perfectly,

    Go to: https://biblefreedom.com/rfid-mark-revealed

    The Bible warns us in the last days that a false prophet will rise up doing miracles to deceive many to take this mark. At all costs, do not take it!

    “Then a third angel followed them, saying with a loud voice, “If anyone worships the beast and his image, and receives his mark on his forehead or on his hand, he himself shall also drink of the wine of the wrath of God, which is poured out full strength into the cup of His indignation. He shall be tormented with fire and brimstone in the presence of the holy angels and in the presence of the Lamb. And the smoke of their torment ascends forever and ever; and they have no rest day or night, who worship the beast and his image, and whoever receives the mark of his name” (Revelation 14:9-11).

    “And He(Jesus) said to me(Apostle John), “It is done! I am the Alpha and the Omega, the Beginning and the End. I will give of the fountain of the water of life freely to him who thirsts” (Revelation 21:6).

    “Jesus answered and said to her, “Whoever drinks of this water will thirst again, but whoever drinks of the water(the Holy Spirit) that I shall give him will never thirst. But the water that I shall give him will become in him a fountain of water springing up into everlasting life” (John 4:13-14).

    “Jesus answered, “Most assuredly, I say to you, unless one is born of water and the Spirit, he cannot enter the kingdom of God. That which is born of the flesh is flesh, and that which is born of the Spirit is spirit. Do not marvel that I said to you, ‘You must be born again.’ (John 3:5-6).

    All religion is man-made. Man can create religion, but no one can create the Holy Spirit that comes from God out of Heaven. Jesus never told us to follow a religion or denomination:

    “Then He(Jesus) said to them all, “If anyone desires to come after Me, let him deny himself, and take up his cross daily, and follow Me” (Luke 9:23).

    You can receive the Spirit of God right now. If you are willing to humble yourself before the Lord, and believe in your heart that God raised Him from the dead on the third day; call out to God and ask Him to forgive your sins, to receive His Holy Spirit. If you are genuine, He is faithful and just to forgive, and He will give you a new heart, a renewing of the mind, restoring everything the devil has stolen from you; making you like a child again, through the sanctification of the Spirit.

    When we receive the Spirit of God, we become born from above, and His seed resides within us. We no longer make a practice of sin, but rather turn away from unrighteousness and receive the righteousness of Christ.

    From that point onward, we must put all our hope and trust in Jesus, and grow to walk in His ways, not straying from the narrow path. For Jesus says,

    “Enter by the narrow gate; for wide is the gate and broad is the way that leads to destruction, and there are many who go in by it. Because narrow is the gate and difficult is the way which leads to life, and there are few who find it” (Matthew 7:13-14).

    “Holy, holy, holy, Lord God Almighty(One God), Who was(Jesus) and is(YHWH) and is to come(Jesus)!” (Revelation 4:8).

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