Rare disease advocates, because of their diseases’ small population of patients, can find it challenging to capture the interest of researchers and drug developers to invest the money, time, and energy that is needed to discover and develop a therapy. One solution is to drive collaborations to leverage the limited resources of foundations and researchers and advance their efforts to a point where drug company may be willing to take over development. Support of Accelerated Research for Niemann-Pick C, or SOAR-NPC, represents such a model. We spoke to Dr. Cristin Davidson, a researcher and project manager for SOAR-NPC, about the organization’s approach, how its tackled various preclinical challenges common to rare diseases, and why the success it has enjoyed should be replicated by others.

RARECast is a weekly series by Daniel S. Levine. Levine is an award-winning business journalist who has reported on the life sciences, economic development, and business policy issues throughout his 25-year career. He founded Levine Media Group in 2013, which produces The Bio Report and RARECast podcasts. Read his full bio here. 

275 thoughts on “RARECast: Innovative Collaboration Model Drive Treatment for Rare Disease”

  1. Pingback: xenical 84
  2. Pingback: proscar generic
  3. Pingback: cost of nolvadex
  4. Pingback: 6 zanaflex
  5. Pingback: Google
  6. Pingback: tadalafil alcohol
  7. Pingback: cialis 10mg uk
  8. Pingback: tadalafil 6mg
  9. Pingback: viagra best buy
  10. Pingback: online viagra
  11. Pingback: Google
  12. Pingback: CANCER
  13. Pingback: butterfly strap on
  14. Pingback: adult stories
  15. Pingback: aksaray escort
  16. Pingback: canada pharmacy
  17. Pingback: latest news
  18. Pingback: happyluke
  19. Pingback: ??????? happyluke
  20. Pingback: male toys
  21. Pingback: sancaktepe escort
  22. Pingback: Microdose Capsules
  23. Pingback: best kegel balls
  24. Pingback: sexual health
  25. Pingback: p spot stimulation
  26. Pingback: Takeout Food
  27. Pingback: fun88
  28. Pingback: p spot massager
  29. Pingback: vibrator review
  30. Pingback: devilbiss 1025ds
  31. Pingback: vagina pump
  32. Pingback: learn more
  33. Pingback: MILF Porn
  34. Pingback: ground lease
  35. Pingback: lotto vip
  36. Pingback: ruay lotto
  37. Pingback: male strokers
  38. Pingback: real feel dildo
  39. Pingback: Bulldogs for sale
  40. Pingback: turk escort
  41. Pingback: streamcomplet
  42. Pingback: site de streaming
  43. Pingback: twitterdownloader
  44. Pingback: pocket pussy
  45. Pingback: w88
  46. Pingback: rabbit thruster
  47. Pingback: pocket vagina
  48. Pingback: 1xbit
  49. Pingback: best in ottawa
  50. Pingback: 토토사이트
  51. Pingback: pmang-no1.com
  52. Pingback: lacquer boxes
  53. Pingback: kleenex
  54. Pingback: NAPHYRONE FOR SALE
  55. Pingback: male sex toy
  56. Pingback: dildos
  57. Pingback: www mp3 juice
  58. Pingback: IT Support Bristol
  59. Pingback: best sex toys
  60. Pingback: Serengeti tours
  61. Pingback: myloweslife.com
  62. Pingback: WEED PUFF BAR
  63. Pingback: taurus gx4
  64. Pingback: sig p938 for sale
  65. Pingback: BUY stiiizy pods
  66. Pingback: magic mushrooms
  67. Pingback: juul pods
  68. Pingback: m&p subcompact
  69. Pingback: Vertise
  70. Pingback: buy ritalin online
  71. Pingback: RissMiner
  72. Pingback: vertigo
  73. Pingback: bitcoin
  74. Pingback: Safari Uganda
  75. Pingback: Uganda Tour
  76. Pingback: beretta pistols
  77. Pingback: raw garden extract
  78. Pingback: BUY WEED ONLINE
  79. Pingback: Rolex Daytona
  80. Pingback: learn more
  81. Pingback: raw garden carts
  82. Pingback: lasix 20 mg daily
  83. Pingback: neurontin 600
  84. Pingback: plaquenil 50 mg
  85. Pingback: modafinil tablets
  86. Pingback: albuterol 100
  87. Pingback: stiizy carts
  88. Pingback: zithromax 250
  89. Pingback: buy plaquenil uk
  90. Pingback: Rentals car Bar
  91. Pingback: what is zithromax
  92. Pingback: getzq.com
  93. Pingback: CableFreeTV
  94. Pingback: NMD News
  95. Pingback: virtual card buy
  96. Pingback: russian last names
  97. Pingback: supreme carts
  98. Pingback: vape juice
  99. Pingback: solar charger
  100. Pingback: Buy Asenlix 30mg
  101. Pingback: lovers kit
  102. Pingback: DailyCBD.com
  103. Pingback: Uganda Tour
  104. Pingback: gbl europe bv
  105. Pingback: ecigarettes
  106. Pingback: Cannabis Oil
  107. Pingback: bathmate
  108. Pingback: uberti dalton
  109. Pingback: best stiiizy pod
  110. Pingback: sig 1911
  111. Pingback: peyote growing kit
  112. Pingback: restaurants
  113. Pingback: sig sauer handguns
  114. Pingback: uca.com.vn
  115. Pingback: online marketing
  116. Pingback: g spot sex toys
  117. Pingback: best clit vibrator
  118. Pingback: huge dildo
  119. Pingback: anal plugs
  120. Pingback: russian bookstore
  121. Pingback: kenya university
  122. Pingback: Honda Valkyrie
  123. Pingback: HELEX PILLS
  124. Pingback: sex toy reviews
  125. Pingback: sbgv245 for sale
  126. Pingback: vape carts
  127. Pingback: gbl solvent