“Mini-Brain” Made of Stem Cells May Help Patients with MECP2 Gene Deletions

In a breakthrough study, the researchers at the University of California, San Diego School of Medicine, have identified a potential way to treat a rare neurological disorder. According to the researchers, a mini-brain made up of the stem cells derived from the patient suffering from the devastating disorder can actually aid in treatment of the disease.

The research team claims to have identified the drug candidate that suppresses the critical genetic alteration, leading to the formation of the dysfunctional cells in the patient. The rare condition, called the MECP2 duplication syndrome, is caused by the “duplication of genetic material in a specific region of the X chromosome that encompasses MECP2 and adjacent genes.”

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