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Business

A total of 240 posts are filed under Business
Prothena Shares Tumble as Company Discontinues AL Amyloidosis Candidate
Rare Daily Staff Prothena said it is discontinuing development of NEOD001, an investigational antibody that was being evaluated for the… Continue Reading
The Global Genes Rare Disease Stock Index Drops 0.66 percent on Week
Markets turned down on Friday as investor shifted attention away from corporate earnings to concerns about inflation. For the week, the… Continue Reading
FDA Grants Modus Therapeutics’ Sevuparin Rare Pediatric Disease Designation for Treatment of Sickle Cell Disease
Rare Daily Staff The U.S. Food and Drug Administration granted Modus Therapeutics’ sevuparin Rare Pediatric Disease designation for the… Continue Reading
NEJM Publishes Promising Bluebird Bio Gene Therapy Data in Beta Thalassemia
Rare Daily Staff Interim data published in the New England Journal of Medicine from two separate studies of Bluebird Bio’s LentiGlobin,… Continue Reading
Shire Rejects Takeda’s $61.9 Billion Bid as Allergan Says It May Jump into the Fray
Rare Daily Staff Rare disease drugmaker Shire said it has rejected a $61.9 billion takeover bid from from Japanese drug giant Takeda as… Continue Reading
FDA Clears for Commercial Use Exemplar Genetics’ Animal Model for Rare Neurodegenerative Disease
Rare Daily Staff The U.S. Food and Drug Administration cleared Intrexon subsidiary Exemplar Genetics’ ExeGen ATM MiniSwine model for… Continue Reading
Ultragenyx and Kyowa Kirin Win FDA Approval for Crysvita to Treat XLH
Rare Daily Staff The U.S. Food and Drug Administration granted approval to Crysvita, Ultragenyx and Kyowa Kirin International’s treatment… Continue Reading