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Business

A total of 354 posts are filed under Business
Mustang Bio Enters License Agreement with St. Jude for X-SCID Gene Therapy
Rare Daily Staff Mustang Bio said it entered into an exclusive worldwide license agreement with St. Jude Children’s Research Hospital for… Continue Reading
FDA Approves Amicus’ Fabry Therapy Galafold
Rare Daily Staff The U.S. Food and Drug Administration today approved Galafold, the first oral medication for the treatment of adults with… Continue Reading
FDA Approves Alynlam’s RNAi Therapeutic for hATTR Amyloidosis
Rare Daily Staff The U.S. Food and Drug Administration approved Alnylam Pharmaceuticals’ Onpattro, a first-of-its-kind RNA interference… Continue Reading
FDA Grants Fast Track Designation to Castle Creek Pharmaceuticals EBS Treatment
Rare Daily Staff The U.S. Food & Drug Administration has granted Fast Track designation to Castle Creek Pharmaceuticals’ CCP-020 for its… Continue Reading
Therachon Raises $60 Million to Advance Achondroplasia Drug and Expand Pipeline
Rare Daily Staff Therachon said it has completed a $60 million financing that will be used to advance its experimental therapy in… Continue Reading
OvaScience and Millendo Agree to Merge to Focus on Rare Endocrine Disease
Rare Daily Staff Millendo Therapeutics and OvaScience said they will merge in a $60 million stock swap that will create a public, late-stage… Continue Reading
U.S. FDA Grants Fast Track Designation for BioCryst’s HAE Drug
Rare Daily Staff The U.S. Food and Drug Administration granted BioCryst Pharmaceuticals Fast Track designation for BCX7353 for the… Continue Reading
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