May 26, 2021
Penn’s Gene Therapy Program Becomes Anchor Tenant of Discovery Labs
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March 18, 2021
Chris Austin Will Leave NCATS to Join VC Firm Flagship Pioneering
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February 20, 2020
FDA Grants Forma Rare Pediatric Disease Designation for SCD Therapy
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February 13, 2020
Synspira and CF Foundation Collaborate to Develop Enzyme Replacement for Malabsorption Syndromes
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February 3, 2020
GW Pharmaceuticals Applies for FDA Approval for Epidiolex to Treat TSC
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January 28, 2020
FTC, N.Y. AG Sue Vyera Pharmaceuticals, Shkreli over Alleged Anticompetitive Scheme
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January 24, 2020
FDA Approves First Treatment for Rare Soft Tissue Cancer
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January 22, 2020
Making the Value Proposition for Rare Disease Therapies
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January 13, 2020
Ultragenyx Reports Positive Topline Results from OTC Deficiency Gene Therapy Study
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January 7, 2020
Deep Genomics Raises $40 Million in Series B Financing
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January 7, 2020
Rhythm CEO to Step Down After FDA Filing
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January 6, 2020
FDA Grants QED Fast Track and Orphan Drug Designations for Rare Cancer Therapy
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