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A total of 467 posts are filed under Business
RegenxBio Bets Its Gene Therapy Technology Provides Competitive Edge
The U.S. Food and Drug Administration recently granted gene therapy developer RegenxBio Orphan Drug designation for its experimental gene… Continue Reading
Mereo BioPharma to Merge with OncoMed Pharmaceuticals
Rare Daily Staff Rare disease drug developer Mereo BioPharma Group and cancer therapeutics developer OncoMed Pharmaceuticals, two… Continue Reading
Abeona Expands Pipeline with Addition of Cystic Fibrosis Gene Therapy
Rare Daily Staff Abeona Therapeutics said it expanded its pipeline with the addition of ABO-401, an experimental gene therapy for cystic… Continue Reading
U.S. Food and Drug Administration Orphan Drug Designations in November 2018
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FDA Grants IntraBio Pediatric Disease Designation for Experimental Niemann-Pick Disease Therapy
Rare Daily Staff The U.S. Food and Drug Administration granted Rare Pediatric Disease designation to IntraBio’s  lead compound series… Continue Reading
FDA Orphan Drug Approvals in 2018
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FDA Approves Catalyst’s LEMS Drug
Rare Daily Staff The U.S. Food and Drug Administration today said it approval Catalyst Pharmaceuticals’ Firdapse, the first treatment for… Continue Reading

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