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A total of 10 posts are filed under Strategy
PhaseRx Cuts Staff, Slows Development in Restructuring
Rare Daily Staff PhaseRx, which is developing mRNA treatments for life-threatening inherited liver diseases in children, that it is… Continue Reading
Abeona Breaks Ground on Gene Therapy Manufacturing Facility in Cleveland
Rare Daily Staff Gene therapy developer Abeona Therapeutics said it broke ground on The Elisa Linton Center for Rare Disease Therapies, a… Continue Reading
Canadian Drug Watchdog Orders Alexion to Lower Price of Soliris, Refund Overcharges
Rare Daily Staff A Patented Medicine Prices Review Board Hearing Panel found Alexion Pharmaceuticals’ rare disease drug Soliris pricing… Continue Reading
Pfizer Rare Disease Spin Out SpringWorks Therapeutics Raises $103 Million
Rare Daily Staff SpringWorks Therapeutics, which Pfizer spun out as an effort to advance certain stalled drugs in  development that have… Continue Reading
University Manufacturing Facility Sees Opportunity in Rare Disease Niche
Rare Daily Staff The University of Tennessee Health Sciences Center is near completion on its effort to convert a warehouse on the eastern… Continue Reading
ProQR Spins Out Amylon Therapeutics as Rare CNS Disease Company
Rare Daily Staff The Netherlands-based ProQR Therapeutics said it has spun out Amylon Therapeutics as a privately-held company focused on… Continue Reading
Alexion to Slash 20 Percent of Staff, Relocate HQ as Part of Restructuring
Rare Daily Staff Rare disease drugmaker Alexion Pharmaceuticals said it would eliminate 20 percent of its workforce and move its… Continue Reading