August 22, 2019
Pfizer to Invest $500 Million in Gene Therapy Manufacturing Facility in North Carolina
Read More
August 22, 2019
Chinook Raises $65 Million to Advance Precision Therapies for Rare Kidney Diseases
Read More
August 22, 2019
Cerecor Receives Fast Track Designation for Rare Metabolic Disorder Therapy
Read More
August 19, 2019
Passage Bio Launches GM1 Natural History Study
Read More
August 19, 2019
FDA Approves Celgene’s Treatment for Rare Bone Cancer
Read More
August 19, 2019
FDA Approves Genentech’s Rozlytrek to Treat Two Rare Cancers
Read More
August 14, 2019
Renovacor Raises $11 Million to Advance Gene Therapy for Rare Cardiovascular Disease
Read More
August 13, 2019
Senate Pressure Grows on Novartis over Gene Therapy Data Manipulation
Read More
August 13, 2019
Jazz Pharmaceuticals Acquires Neurological Drug Developer
Read More
August 12, 2019
ProQR Gets FDA Clearance to Start Clinical Trial to Treat Rare Eye Disease
Read More
August 12, 2019
Immunic Says First Patient Enrolled in Proof-of-Concept Trial for Rare Liver Disease Therapy
Read More
August 9, 2019
Giving Voice to Patients through Data
Read More
Load More
X