February 22, 2019
Ionis CEO Stanley Crooke Discusses Success as a Platform Technology Company
Read More
February 21, 2019
Avexis Plans $60 Million Expansion of Manufacturing Facility in North Carolina
Read More
February 19, 2019
Nestle Health Sciences Exercises Option for Codexis PKU Treatment
Read More
February 15, 2019
Passage Bio Raises $115.5 Million to Develop Gene Therapies for CNS Disease
Read More
February 12, 2019
Neurogene Raises $68.5 to Advance Gene Therapies for Rare Neurological Diseases
Read More
February 12, 2019
FDA Grants Clementia Rare Pediatric Disease Designation by FOP Drug
Read More
February 7, 2019
FDA Approves Sanofi’s Cablivi for Rare Blood-Clotting Disorder aTTP, the First of a…
Read More
January 14, 2019
Pharma R&D Returns Fall to Lowest Level in Nine Years
Read More
January 4, 2019
How Patient-Led Collaborations Are Transforming Rare Disease Drug Discovery and Development
Read More
July 26, 2018
Viagra Inventor Raises $10M to Accelerate Rare Disease Drug Discovery with AI
Read More
June 29, 2018
Sanofi Genzyme Creates Challenge to Find Digital Technologies to Speed Rare Disease Diagnoses
Read More
June 18, 2018
FDA Removes Clinical Hold on Solid Biosciences Experimental DMD Gene Therapy
Read More
Load More