
Caribou Reports Positive Initial Data for Gene-Edited Allogeneic CAR-T Cell Therapy
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Takeda Notifies Ovid of Delays in Pivotal Study of Therapy for Rare Epilepsies
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FDA Extends PDUFA Date for Amicus’ Experimental Therapy to Treat Pompe Disease
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Mereo Reports Positive Data from Phase 2 Study of Alvelestat in AATD-related Emphysema
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FDA Lifts Clinical Hold on LogicBio’s Trial in Pediatric Patients with Methylmalonic Acidemia
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Ultomiris Met Primary Endpoint in Phase 3 Trial in Adults with Rare Autoimmune Condition NMOSD<br><br><em>Rare Daily Staff</em>
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