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Global Genes

A total of 299 posts are filed under Global Genes
Hacking Rare Disease
As a teenager, Bill Paseman worked with his father in the refineries around the Houston area. He remembers remarking to him at the time that… Continue Reading
Programming Stem Cells to Protect Neurons in ALS
BrainStorm Cell Therapeutics is developing innovative, autologous stem cell therapies for debilitating neurodegenerative diseases such as… Continue Reading
Global Genes Relaunches RareUniversity
Rare Daily Staff RareUniversity, originally launched in 2016, has moved to a new platform to improve its focus and better address knowledge… Continue Reading
How Bo Bigelow Became a Hunter-Gatherer
Bo Bigelow is on a quest to find 68 patients. Bigelow, chairman of the Foundation for USP7-Related Diseases, needs to find 68 more patients… Continue Reading
Why a Topical, Off-the-Shelf, Gene Therapy May Hold Promise for a Rare Skin Condition
Dystrophic epidermolysis bullosa is a rare, genetic disease that affects the skin and other organs. People with the condition have skin that… Continue Reading
Are Orphan Drugs Losing their Luster?
The orphan drug market is experiencing strong growth, but there are signs that pricing pressures may be impacting the sector, raising… Continue Reading
An Ironman Champion with Cystic Fibrosis Discusses her Changing Relationship with Her Disease
Lisa Bentley spent 20 years competing as a professional athlete, although early in her career she kept secret that she suffered from the… Continue Reading

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