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Innovation

A total of 428 posts are filed under Innovation
Genentech to Highlight Actemra and Rituxan Data at EULAR Annual Congress
Various new data on Genentech’s Actemra (tocilizumab) and Rituxan (rituximab) will be presented at the 2017 European League Against… Continue Reading
Video: How Children’s Hospital of Philadelphia is Helping Leukodystrophy Patients
Leukodystrophies are inherited disorders of the white matter of the brain and spinal cord that can cause problems with movement, speaking,… Continue Reading
Castle Creek Announces First Patient Enrolled in DELIVERS Study of Diacerein 1% Ointment for Epidermolysis Bullosa Simplex
Castle Creek Pharmaceuticals (CCP), a global company dedicated to delivering transformative therapies to patients with orphan dermatologic… Continue Reading
CD Access to Provide Special Access Program for Duchenne Muscular Dystrophy Patients in Canada
 CD Access is a new nonprofit that provides patients access to drugs and therapies that are currently unavailable through clinical trial… Continue Reading
Amicus Therapeutics Receives Rare Pediatric Disease Designation for SD-101 for Patients with Epidermolysis Bullosa
 Amicus Therapeutics, Inc.(link is external) (Nasdaq:FOLD), has received Rare Pediatric Disease designation from the U.S. Food and Drug… Continue Reading
ProQR Receives Fast Track Designation from the FDA for QR-110 for Leber’s Congenital Amaurosis Type 10
 ProQR Therapeutics N.V.(Nasdaq:PRQR) today announced that it received Fast Track designation from the U.S. Food and Drug… Continue Reading
IPF Patients Treated with Ofev® VS Placebo Were Twice as Likely to Have Improved or Stable Lung Function
Separate subgroup analysis demonstrates long-term efficacy of Ofev® in slowing disease progression is maintained for up to 96 weeks in IPF… Continue Reading
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