October 8, 2021
Alnylam becomes a partner in the Medicines Manufacturing Innovation Centre
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March 24, 2021
Horizon Therapeutics Launches Prize with MIT to Advance Solutions for the Rare Disease Community
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February 18, 2021
FDA Approves First-of-Its-Kind Implant to Treat Rare Bone Disease as a Humanitarian Use Device
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January 13, 2021
Study Suggests Genetic Editing Could Correct Rare Disease that Causes Rapid Aging
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July 7, 2020
Gene Writing Technology Company Tessera Therapeutics Emerges from Stealth
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March 11, 2020
Amicus Opens New Global Research and Gene Therapy Center of Excellence
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March 2, 2020
World Economic Forum Proposes Framework for Sharing Genomic Data to Diagnose and Treat Rare Disease
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February 24, 2020
Cell and Gene Therapy Companies Raised $6.4 Billion in 2019 for Rare Disease
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February 21, 2020
FDA Grants BioMarin Priority Review for Hemophilia A Gene Therapy
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February 19, 2020
Univercells Scores Up to $54 Million Investment from KKR
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February 18, 2020
First UK Patients Begin Gene Therapy Treatment for Blindness through NHS
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February 7, 2020
Crowdsourcing Therapeutic Approaches for an Ultra-Rare Disease
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