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Innovation

A total of 438 posts are filed under Innovation
New Rare Disease Center Opens in U.K. to Treat Rare Genetic and Skin Conditions
Rare Daily Staff The Rare Diseases Centre at St Thomas’ Hospital, a first-of-its-kind center in the United Kingdom to treat patients with… Continue Reading
Learning from Rare Diseases
Daniel S. Levine   Matt Wilsey has liked to make the case that one justification for investing in rare disease research is that through it,… Continue Reading
Grace Science Foundation and Stanford University Create Biobank for Ultra-Rare NGLY1 Deficiency
Rare Daily Staff The Grace Science Foundation and a clinical research team from Stanford University have created an open source biobank of… Continue Reading
Rare Disease Report: Is Sjorgen Syndrome a Rare Disease?
By James Radke at Rare Disease Report According to the Genetic and Rare Diseases Information Center (GARD) at the National Institutes of… Continue Reading
New Data Show Survival Improvement with Adcetris in Hodgkin Lymphoma Patients
by Mathew Shanley for Rare Disease Report Earlier today, Takeda and Seattle Genetics announced promising results from its Phase 3 ECHELON-1… Continue Reading
CheckRare: FDA Approves Haegarda to Treat HAE
The U.S. Food and Drug Administration today approved Haegarda, the first C1 Esterase Inhibitor (Human) for subcutaneous administration to… Continue Reading
Patient-Inspired Research Uncovers New Link to Rare Disorder
Meeting a young patient with Zellweger syndrome, a rare, life-threatening genetic disease, started a scientific investigation that… Continue Reading
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