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Innovation

A total of 567 posts are filed under Innovation
A STAR Is Born
When Jessica Klein-Foglio’s and Michael Foglio’s son Ben was diagnosed in 2017 with Salla disease, an ultra-rare lysosomal disorder, the… Continue Reading
Collaboration Identifies Biomarker Evidence in Castleman Disease
Rare Daily Staff The Castleman Disease Collaborative Network and Medidata said they discovered new Castleman patient subgroups, based on… Continue Reading
Orchard Therapeutics Reports Clinical Proof-of-Concept Data for X-CGD Gene Therapy at ASH
Rare Daily Staff Orchard Therapeutics said it presented the first demonstration that its experimental gene therapy OTL-102 for the treatment… Continue Reading
RegenxBio Bets Its Gene Therapy Technology Provides Competitive Edge
  The U.S. Food and Drug Administration recently granted gene therapy developer RegenxBio Orphan Drug designation for its experimental gene… Continue Reading
The 100,000 Genomes Project Reaches Its Goal
Rare Daily Staff The 100,000 Genomes Project, led by Genomics England in partnership with NHS England, has reached its goal of sequencing… Continue Reading
A $400 Million Investment Seeks to Turn Ireland into a Genomics Hub
Rare Daily Staff The Ireland Strategic Investment Fund, WuXi NextCODE, and Irish life sciences company Genomics Medicine Ireland outlined a… Continue Reading
Now Comes the Hard Part
Earlier this month during Novartis’ R&D Day, Dave Lennon caught the attention of the payer community when he said that the company’s… Continue Reading
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