Subscribe to
this category
r

Innovation

A total of 398 posts are filed under Innovation
RDR: Cydan Announces Acquisition of Its Rare Disease Spin-out Vtesse
The orphan drug accelerator company, Cydan Development announces that Sucampo Pharmaceuticals Inc. has acquired Vtesse Inc. Cydan… Continue Reading
Teva Announces FDA Approval of AUSTEDO™ (deutetrabenazine) Tablets for the Treatment of Chorea Associated with Huntington’s Disease
Teva Pharmaceutical Industries Ltd. (NYSE and TASE: TEVA) today announced that the U.S. Food and Drug Administration (FDA) has approved… Continue Reading
PROQR
ProQR Appoints David M. Rodman, MD as Chief Development Strategy Officer
ProQR Therapeutics N.V. (Nasdaq: PRQR) today announced that it appointed David M. Rodman, MD as Chief Development Strategy Officer. Dr.… Continue Reading
Glut1DS
New Clinical Trial Announced for Patients with Glucose Transporter Type-1 Deficiency Syndrome
For Patients With Glucose Transporter Type-1 Deficiency Syndrome (Glut1 DS) Experiencing Movement Disorders Learn about a Phase 3 clinical… Continue Reading
Jaipur Doctor to be Part of Drafting Policy on Treating Rare Disease
(SOURCE)   JAIPUR: A city-based doctor, who has introduced ‘enzyme replacement therapy’ in JK Lon hospital will play key role in… Continue Reading
Rare_Skin_Cancer
FDA Approves First Treatment for Rare Form of Skin Cancer
The U.S. Food and Drug Administration today granted accelerated approval to Bavencio (avelumab) for the treatment of adults and pediatric… Continue Reading
Eyes_Gene_Therapy
Allergan Signs Deal with Editas for Gene-Editing-Based Eye Treatments
Allergan plc said on Tuesday it would get exclusive access and the option to license up to five of Editas Medicine Inc’s experimental… Continue Reading
be-a-guest-blogger

Follow us on Twitter

Upcoming Events

Sep 14

Rare Patient Advocacy Summit

September 14 @ 8:00 am - 5:30 pm
Sep 14

Rare Partnering 2017

September 14 @ 8:00 am - 5:00 pm
Sep 15

Rare Patient Advocacy Summit

September 15 @ 8:00 am - 4:00 pm
Sep 15

Community Nominated Ceremony and Reception

September 15 @ 4:30 pm - 9:00 pm
Sep 16

Corporate Alliance

September 16 @ 9:00 am - 12:00 pm
Sep 16

Rare Day of Beauty

September 16 @ 12:30 pm - 4:00 pm
Sep 16

Tribute to Champions of Hope

September 16 @ 5:30 pm - 10:30 pm