May 12, 2022
At a Crossroad for Innovation in Rare Disease
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May 5, 2022
What Does it Take to Become a Research-Ready Organization?
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April 20, 2022
Horizon and MIT Solve Announce Second Annual Rare Disease Global Innovation Challenge
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February 11, 2022
Simplifying RNA Editing for Treating Genetic Diseases
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December 20, 2021
2021 Platforms of Hope – Realizing the Potential of Genetic Medicines
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October 8, 2021
Alnylam becomes a partner in the Medicines Manufacturing Innovation Centre
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March 24, 2021
Horizon Therapeutics Launches Prize with MIT to Advance Solutions for the Rare Disease Community
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February 18, 2021
FDA Approves First-of-Its-Kind Implant to Treat Rare Bone Disease as a Humanitarian Use Device
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January 13, 2021
Study Suggests Genetic Editing Could Correct Rare Disease that Causes Rapid Aging
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July 7, 2020
Gene Writing Technology Company Tessera Therapeutics Emerges from Stealth
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March 11, 2020
Amicus Opens New Global Research and Gene Therapy Center of Excellence
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March 2, 2020
World Economic Forum Proposes Framework for Sharing Genomic Data to Diagnose and Treat Rare Disease
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