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A total of 148 posts are filed under Business
Sanofi Genzyme Creates Challenge to Find Digital Technologies to Speed Rare Disease Diagnoses
Rare Daily Staff Sanofi Genzyme has issued a call for submissions for its Rare Innovation Challenge, an effort to find innovative digital… Continue Reading
FDA Removes Clinical Hold on Solid Biosciences Experimental DMD Gene Therapy
Rare Daily Staff The U.S. Food and Drug Administration has lifted the clinical hold on Solid Biosciences’ phase 1/2 clinical trial for its… Continue Reading
Catalyst Pharmaceuticals Receives 2017 Beacon Council Award for Contributions in Life Sciences & Healthcare
Catalyst Pharmaceuticals, Inc. (Nasdaq:CPRX), a biopharmaceutical company focused on developing and commercializing innovative therapies for… Continue Reading
Teva Showcases CNS Portfolio at 69th Annual Meeting of the American Academy of Neurology
Teva Pharmaceutical Industries Ltd., (NYSE and TASE: TEVA) today announced data for five of the Company’s innovative therapies for central… Continue Reading
Horizon Pharma plc Announces FDA Approval to Expand the Age Range for RAVICTI® to People with Urea Cycle Disorders Ages Two Months +
Horizon Pharma plc (NASDAQ:HZNP), a biopharmaceutical company focused on improving patients’ lives by identifying, developing, acquiring… Continue Reading
Promising Week for Treatment of Form of Batten Disease: Approvals Granted by FDA and Europe’s CHMP
Significant progress was made last week for those suffering from Batten Disease (CLN2), a form of lysosomal storage disorder characterized… Continue Reading
BioPharma Dive: 5 Trends Shaping Rare Disease Drug Development
Story by Ned Pagliarulo Amid ongoing scrutiny of rising prescription drug costs, a three decade-old law has become a new flash point in the… Continue Reading

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