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A total of 143 posts are filed under Business
Promising Week for Treatment of Form of Batten Disease: Approvals Granted by FDA and Europe’s CHMP
Significant progress was made last week for those suffering from Batten Disease (CLN2), a form of lysosomal storage disorder characterized… Continue Reading
BioPharma Dive: 5 Trends Shaping Rare Disease Drug Development
Story by Ned Pagliarulo Amid ongoing scrutiny of rising prescription drug costs, a three decade-old law has become a new flash point in the… Continue Reading
RDR: Cydan Announces Acquisition of Its Rare Disease Spin-out Vtesse
The orphan drug accelerator company, Cydan Development announces that Sucampo Pharmaceuticals Inc. has acquired Vtesse Inc. Cydan… Continue Reading
Teva Announces FDA Approval of AUSTEDO™ (deutetrabenazine) Tablets for the Treatment of Chorea Associated with Huntington’s Disease
Teva Pharmaceutical Industries Ltd. (NYSE and TASE: TEVA) today announced that the U.S. Food and Drug Administration (FDA) has approved… Continue Reading
PROQR
ProQR Appoints David M. Rodman, MD as Chief Development Strategy Officer
ProQR Therapeutics N.V. (Nasdaq: PRQR) today announced that it appointed David M. Rodman, MD as Chief Development Strategy Officer. Dr.… Continue Reading
Regenerative_Cell_Thera[y
InGeneron Completes Strategic Financing from Sanford Health to Advance Regenerative Cell Therapies
 InGeneron Inc., a regenerative medicine and cell therapy company, announces that Sanford Health, one of the largest integrated healthcare… Continue Reading
Akcea Therapeutics’ Volanesorsen Study Meets Primary Endpoint of Reducing Triglyceride Levels in Patients with Familial Chylomicronemia Syndrome (FCS)
Akcea Therapeutics, a wholly owned subsidiary of Ionis Pharmaceuticals, Inc. (NASDAQ: IONS), today announced that the pivotal Phase 3… Continue Reading
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