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A total of 107 posts are filed under Business
Fierce Biotech: Roivant and Plexcera Launch Rare Disease Focused Spinout
Roivant Sciences and Plexcera Therapeutics have today launched a new biotech company with a singular focus on the ultrarare condition known… Continue Reading
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Marathon Pharmaceuticals Announces Submission of Deflazacort New Drug Application to the FDA
Marathon Pharmaceuticals, LLC, a biopharmaceutical company developing treatments for rare diseases, today announced it has submitted a New… Continue Reading
Takeda to Invest $65M in Ultragenyx under Rare Disease Drug Collaboration
SOURCE Ultragenyx Pharmaceutical will license and co-develop at least one and possibly up to six candidates from Takeda Pharmaceutical,… Continue Reading
Intercept’s Liver Drug Wins FDA Approval To Treat Rare Disease
The FDA ended a busy week by giving a thumbs-up late Friday to obeticholic acid as a treatment for primary biliary cirrhosis, a rare… Continue Reading
Akari Therapeutics Gets Positive Opinion For Orphan Drug Status For Coversin In EU For Guillain Barré Syndrome Treatment
Story source. By R. Chandrasekaran , Benzinga Staff Writer Akari Therapeutics NASDAQAKTX revealed that the European Medicines Agency… Continue Reading
Screen Shot 2016-05-12 at 7.36.15 PM More Than 560 Medicines in Development for Rare Diseases
Rare diseases, when taken together, are not that rare at all. In fact, 30 million Americans, or 10 percent of the population, have one of… Continue Reading
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Audentes Therapeutics and the University of Pennsylvania Announce Collaboration to Develop AAV Gene Therapy for Severe Liver Disease
Audentes Therapeutics, Inc., a biotechnology company focused on developing and commercializing gene therapy products for patients suffering… Continue Reading

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