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A total of 109 posts are filed under Business
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Early Stage Investment by CureDuchenne Ventures, LLC Enabled Bamboo Therapeutics to Accelerate Development of a Gene Therapy for Duchenne Muscular Dystrophy
Today, Pfizer Inc. announced its acquisition of Bamboo Therapeutics in a deal worth up to $645 million. Bamboo Therapeutics is an… Continue Reading
Vtesse Secures Support for Product Development and Ongoing Clinical
Vtesse, Inc., a company committed to developing drugs that will benefit patients with extremely rare, life-threatening diseases, announced… Continue Reading
Fierce Biotech: Roivant and Plexcera Launch Rare Disease Focused Spinout
Roivant Sciences and Plexcera Therapeutics have today launched a new biotech company with a singular focus on the ultrarare condition known… Continue Reading
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Marathon Pharmaceuticals Announces Submission of Deflazacort New Drug Application to the FDA
Marathon Pharmaceuticals, LLC, a biopharmaceutical company developing treatments for rare diseases, today announced it has submitted a New… Continue Reading
Takeda to Invest $65M in Ultragenyx under Rare Disease Drug Collaboration
SOURCE Ultragenyx Pharmaceutical will license and co-develop at least one and possibly up to six candidates from Takeda Pharmaceutical,… Continue Reading
Intercept’s Liver Drug Wins FDA Approval To Treat Rare Disease
The FDA ended a busy week by giving a thumbs-up late Friday to obeticholic acid as a treatment for primary biliary cirrhosis, a rare… Continue Reading
Akari Therapeutics Gets Positive Opinion For Orphan Drug Status For Coversin In EU For Guillain Barré Syndrome Treatment
Story source. By R. Chandrasekaran , Benzinga Staff Writer Akari Therapeutics NASDAQAKTX revealed that the European Medicines Agency… Continue Reading