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A total of 30 posts are filed under Genetics
Amicus Therapeutics Receives Rare Pediatric Disease Designation for SD-101 for Patients with Epidermolysis Bullosa
 Amicus Therapeutics, Inc.(link is external) (Nasdaq:FOLD), has received Rare Pediatric Disease designation from the U.S. Food and Drug… Continue Reading
The Alliance for Regenerative Medicine Releases 2016 Annual Data Report, Highlighting Sector Trends and Metrics
The Alliance for Regenerative Medicine (ARM) today announced the release of its 2016 annual data report, offering an in-depth look at trends… Continue Reading
Saudi Gene Hunters Comb Country’s DNA to Prevent Rare Diseases
by Jocelyn Kaiser at Science Magazine In a hospital conference room here in Saudi Arabia’s capital, a lieutenant colonel in the Saudi… Continue Reading
After Three Decades, Gene Therapy Comes of Age
By JEFF ST. CLAIR Gene therapy was once viewed as a promising new way to treat many incurable diseases — until a tragic death occurred… Continue Reading
Genome Study Offers New Hope For Rare Kids
An international team involving University of Queensland researchers has used advanced genome sequencing to diagnose 30 patients with… Continue Reading
Stem Cell Gene Therapy Shows Promise In Treating Patients With Rare Immunodeficiency Disorder
According to scientists from the National Institute of Allergy and Infectious Diseases, gene therapy can safely restore the immunity of… Continue Reading
India Raring to Make its Mark in the Rare Disease Market
With one-third of all new approved drugs over the past five years in the US addressing rare diseases, the last decade is said to have been… Continue Reading
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