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Science & Technology

A total of 153 posts are filed under Science & Technology
The Atlantic: What If (Almost) Every Gene Affects (Almost) Everything?
By Ed Yong (SOURCE) In 1999, a group of scientists scoured the genomes of around 150 pairs of siblings in an attempt to find genes that are… Continue Reading
Dalhousie Researcher Studying Drug to Combat Fabry Disease
A simple pill that switches off a genetic trigger could potentially provide a powerful treatment for Fabry disease, a rare disorder that… Continue Reading
Genentech to Highlight Actemra and Rituxan Data at EULAR Annual Congress
Various new data on Genentech’s Actemra (tocilizumab) and Rituxan (rituximab) will be presented at the 2017 European League Against… Continue Reading
Castle Creek Announces First Patient Enrolled in DELIVERS Study of Diacerein 1% Ointment for Epidermolysis Bullosa Simplex
Castle Creek Pharmaceuticals (CCP), a global company dedicated to delivering transformative therapies to patients with orphan dermatologic… Continue Reading
Amicus Therapeutics Receives Rare Pediatric Disease Designation for SD-101 for Patients with Epidermolysis Bullosa
 Amicus Therapeutics, Inc.(link is external) (Nasdaq:FOLD), has received Rare Pediatric Disease designation from the U.S. Food and Drug… Continue Reading
ProQR Receives Fast Track Designation from the FDA for QR-110 for Leber’s Congenital Amaurosis Type 10
 ProQR Therapeutics N.V.(Nasdaq:PRQR) today announced that it received Fast Track designation from the U.S. Food and Drug… Continue Reading
IPF Patients Treated with Ofev® VS Placebo Were Twice as Likely to Have Improved or Stable Lung Function
Separate subgroup analysis demonstrates long-term efficacy of Ofev® in slowing disease progression is maintained for up to 96 weeks in IPF… Continue Reading
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