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Science & Technology

A total of 117 posts are filed under Science & Technology
New Study Being Run for Catalyst Pharma for Patients with Congenital Myasthenic Syndromes (CMS)
Patients may now be eligible to participate in a new research study evaluating an investigational medicine for the treatment of CMS. WHY a… Continue Reading
Rare Disease Community Joins to Launch the Collaborative Trajectory Analysis Project Advancing Clinical Trial Design for DMD
The next wave in tackling Duchenne Muscular Dystrophy is getting a boost from a collaboration of nonprofit organizations, biopharmaceutical… Continue Reading
CBS Sunday Morning Presents Story on MLD with the The Calliope Joy Foundation
This past Sunday, CBS aired a meaningful segment on late infantile metachromatic leukodystrophy and some of the families who are affected… Continue Reading
Andrew Spear for The Washington Post via Getty
Dr House Goes Digital as IBM’s Watson Diagnoses Rare Diseases
Original Source By Paul Marks Doctor House is going electronic. Medics charged with diagnosing the kind of extremely rare diseases that… Continue Reading
SELLAS™ Life Sciences Announces Positive Interim Phase II Results from its WT1 Immunotherapeutic Anti-cancer Treatment in Multiple Myeloma Patients
SELLAS Life Sciences Group (SELLAS or the Company), a late-stage biopharmaceutical company focused on the development of novel cancer… Continue Reading
University of Arkansas to Lead $1.4M Study on Rare Disease
The University of Arkansas will use a $1.4 million grant to study the origin of Leigh’s Disease, a rare and incurable disease that affects… Continue Reading
FDA Helps Fund 21 Early Phase Trials for Rare Disease Treatments
(Source) by Zachary Brennan The US Food and Drug Administration (FDA) on Monday announced it is awarding $23 million in research grants for… Continue Reading