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Science & Technology

A total of 123 posts are filed under Science & Technology
RDR: FDA Approves Rubraca (rucaparib) for Rare Ovarian Cancer
The FDA has approved the orphan drug Rubraca (rucaparib) to treat women with advanced ovarian cancer who have been treated with 2 or more… Continue Reading
Vote Now for MyGene2 in the Open Science Prize!
  MyGene2 is a free, family-friendly platform for families with rare diseases, clinicians, and researchers to publicly share health and… Continue Reading
Clinically Meaningful Data for Oral Ninteddanib in Mesothelioma Presented at World Conference on Lung Cancer
Boehringer Ingelheim today announced that the LUME-Meso Phase II trial in patients with unresectable malignant pleural mesothelioma (MPM)… Continue Reading
Rare Disease Report: FDA Fully Approves Iclusig for Chronic Myeloid Leukemia
(Source) The FDA has fully approved ARIAD Pharmaceuticals’ Iclusig (ponatinib) for the treatment of adult patients with chronic phase,… Continue Reading
N. Scott Adzick, MD, CHOP’s Surgeon-in-Chief, Recognized by Congenital Hyperinsulinism International (CHI)
As surgeon-in-chief at Children’s Hospital of Philadelphia (CHOP), and founder and director of the hospital’s Center for Fetal… Continue Reading
Repurposing Drugs for Rare Diseases: Collaboration is Key
by Tim Hoctor, Vice President, Corporate R&D Professional Services, Elsevier (SOURCE) The statistics are sobering: an estimated 350… Continue Reading
New Study Being Run for Catalyst Pharma for Patients with Congenital Myasthenic Syndromes (CMS)
Patients may now be eligible to participate in a new research study evaluating an investigational medicine for the treatment of CMS. WHY a… Continue Reading

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