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Science & Technology

A total of 150 posts are filed under Science & Technology
Castle Creek Announces First Patient Enrolled in DELIVERS Study of Diacerein 1% Ointment for Epidermolysis Bullosa Simplex
Castle Creek Pharmaceuticals (CCP), a global company dedicated to delivering transformative therapies to patients with orphan dermatologic… Continue Reading
Amicus Therapeutics Receives Rare Pediatric Disease Designation for SD-101 for Patients with Epidermolysis Bullosa
 Amicus Therapeutics, Inc.(link is external) (Nasdaq:FOLD), has received Rare Pediatric Disease designation from the U.S. Food and Drug… Continue Reading
ProQR Receives Fast Track Designation from the FDA for QR-110 for Leber’s Congenital Amaurosis Type 10
 ProQR Therapeutics N.V.(Nasdaq:PRQR) today announced that it received Fast Track designation from the U.S. Food and Drug… Continue Reading
IPF Patients Treated with Ofev® VS Placebo Were Twice as Likely to Have Improved or Stable Lung Function
Separate subgroup analysis demonstrates long-term efficacy of Ofev® in slowing disease progression is maintained for up to 96 weeks in IPF… Continue Reading
Parents of Children With Rare Disease Move Researchers to Connecticut
Story by Stephen Singer at The Hartford Courant Gayle Temkin spends her days at Solomon Schechter Day School, where she occupies a small,… Continue Reading
FDA Approves Genentech’s Actemra (Tocilizumab) for Giant Cell Arteritis
Genentech, a member of the Roche Group announced today that the U.S. Food and Drug Administration (FDA) has approved… Continue Reading
FDA Grants Priority Review Status to Ultragenyx
Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE), a biopharmaceutical company focused on the development of novel products for rare and… Continue Reading
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