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Science & Technology

A total of 163 posts are filed under Science & Technology
Study Finds Facial Analysis Software Able to Identify Patients with Williams-Beuren Syndrome
Rare Daily Staff A new study has shown that researchers have successfully used facial analysis technology and clinical information to… Continue Reading
Failed Drug May Have New Life as Treatment for Rare Motor Neuron Disease
Rare Daily Staff A team of international researchers have identified a failed drug first discovered in the 1980s as a potential new… Continue Reading
Study Could Lead to Gene Editing Therapy for Inherited Blood Disorders
Rare Daily Staff A study that determined how naturally-occurring gene mutations can counter the effects of inherited blood diseases has… Continue Reading
Generation Bio Raises $100 Million to Advance Re-Dosable Gene Therapy
Rare Daily Staff Generation Bio said it closed a $100 million series B financing to advance to the clinic its first two therapeutics… Continue Reading
Shire, Microsoft, and Eurodis Form Alliance to Accelerate Diagnosis of Rare Diseases
Rare Daily Staff Rare disease drugmaker Shire, Microsoft, and the rare disease patient organization Eurodis-Rare Diseases Europe have formed… Continue Reading
FDA Grants MeiraGTx Rare Pediatric Disease Designation to Gene Therapy for Eye Disease
Rare Daily Staff The U. S. Food and Drug Administration granted rare pediatric disease designation to MeiraGTx’s gene therapy product… Continue Reading
Solid Biosciences Initiates Clinical Trial for Gene Transfer Candidate in Duchenne
Rare Daily Staff Solid Biosciences said that it has initiated clinical trial activities for SGT-001, the company’s lead microdystrophin… Continue Reading
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