Subscribe to
this category
r

Research

A total of 197 posts are filed under Research
Jaipur Doctor to be Part of Drafting Policy on Treating Rare Disease
(SOURCE)   JAIPUR: A city-based doctor, who has introduced ‘enzyme replacement therapy’ in JK Lon hospital will play key role in… Continue Reading
Rare_Skin_Cancer
FDA Approves First Treatment for Rare Form of Skin Cancer
The U.S. Food and Drug Administration today granted accelerated approval to Bavencio (avelumab) for the treatment of adults and pediatric… Continue Reading
Eyes_Gene_Therapy
Allergan Signs Deal with Editas for Gene-Editing-Based Eye Treatments
Allergan plc said on Tuesday it would get exclusive access and the option to license up to five of Editas Medicine Inc’s experimental… Continue Reading
Regenerative_Cell_Thera[y
InGeneron Completes Strategic Financing from Sanford Health to Advance Regenerative Cell Therapies
 InGeneron Inc., a regenerative medicine and cell therapy company, announces that Sanford Health, one of the largest integrated healthcare… Continue Reading
The Alliance for Regenerative Medicine Releases 2016 Annual Data Report, Highlighting Sector Trends and Metrics
The Alliance for Regenerative Medicine (ARM) today announced the release of its 2016 annual data report, offering an in-depth look at trends… Continue Reading
Epidermolysis Bullosa
New Hope For Epidermolysis Bullosa Patients with Investigational Therapy from Castle Creek Pharmaceuticals
Castle Creek Pharmaceuticals (CCP), a global company dedicated to delivering transformative therapies to patients with dermatologic and… Continue Reading
Akcea Therapeutics’ Volanesorsen Study Meets Primary Endpoint of Reducing Triglyceride Levels in Patients with Familial Chylomicronemia Syndrome (FCS)
Akcea Therapeutics, a wholly owned subsidiary of Ionis Pharmaceuticals, Inc. (NASDAQ: IONS), today announced that the pivotal Phase 3… Continue Reading
be-a-guest-blogger

Follow us on Twitter

Upcoming Events

Sep 14

Rare Patient Advocacy Summit

September 14 @ 8:00 am - 5:30 pm
Sep 14

Rare Partnering 2017

September 14 @ 8:00 am - 5:00 pm
Sep 15

Rare Patient Advocacy Summit

September 15 @ 8:00 am - 4:00 pm
Sep 15

Community Nominated Ceremony and Reception

September 15 @ 4:30 pm - 9:00 pm
Sep 16

Corporate Alliance

September 16 @ 9:00 am - 12:00 pm
Sep 16

Rare Day of Beauty

September 16 @ 12:30 pm - 4:00 pm
Sep 16

Tribute to Champions of Hope

September 16 @ 5:30 pm - 10:30 pm