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Research

A total of 213 posts are filed under Research
IPF Patients Treated with Ofev® VS Placebo Were Twice as Likely to Have Improved or Stable Lung Function
Separate subgroup analysis demonstrates long-term efficacy of Ofev® in slowing disease progression is maintained for up to 96 weeks in IPF… Continue Reading
Parents of Children With Rare Disease Move Researchers to Connecticut
Story by Stephen Singer at The Hartford Courant Gayle Temkin spends her days at Solomon Schechter Day School, where she occupies a small,… Continue Reading
Abeona Therapeutics Announces New Updates on Sanfilippo Syndrome Clinical Trial
Abeona Therapeutics Inc. (NASDAQ:ABEO), a leading clinical-stage biopharmaceutical company focused on developing novel gene therapies for… Continue Reading
National Leiomyosarcoma Foundation and Rare Cancer Research Foundation Team Up to Study Tumor Tissue
The National Leiomyosarcoma Foundation announces an exciting new collaborative partnership with the Rare Cancer Research Foundation (RCRF),… Continue Reading
jCyte Receives Regenerative Medicine Advanced Therapy Designation
Cell therapy company jCyte announced that the U.S. Food & Drug Administration (FDA) has granted Regenerative Medicine Advanced Therapy… Continue Reading
Abeona Therapeutics Receives Regulatory Approval to Initiate Clinical Trial in Australia with ABO-102 Gene Therapy For Patients with MPS IIIA
Clinical Trial Notification (CTN) Enables Initiation at 3rd Global Site and Accelerates Enrollment in the ABO-102 MPS IIIA Gene Therapy… Continue Reading
Introducing SideEQ: A Free Tool That Helps You Manage Cancer Treatment Side Effects
SideEQ is a free, interactive platform which enables people living with cancer to track and manage their side effects so they can improve… Continue Reading
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