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A total of 242 posts are filed under Research
Thinking Ahead
When the European Medicines Agency approved Myozyme in 2006, Genzyme’s enzyme replacement therapy for the lysosomal storage disorder… Continue Reading
FDA Awards Five Grants to Advance Development of Pediatric Medical Devices
Rare Daily Staff The U.S. Food and Drug Administration said that it has awarded five grants totaling up to $6 million per year over the next… Continue Reading
Blood Test Could Help Diagnose Kids with Autism
Rare Daily Staff Investigators at the UC Davis MIND Institute and NeuroPointDX said they have identified a group of blood metabolites that… Continue Reading
Researchers Discover Mechanism that Reduces Neurodegeneration in Huntington’s Disease
Rare Daily Staff Researchers at the University of Cologne’s Cluster of Excellence for Aging Research said that they identified a system… Continue Reading
Researchers Develop Potential Gene Therapy for Rare Disease that Causes Blindness
Rare Daily Staff Researchers reported that a novel gene therapy that halts vision loss in a canine model of autosomal dominant retinitis… Continue Reading
Australian Researchers Develop Method That Could Make Cell Therapy Viable for CF
Rare Daily Staff Researchers at the University of Adelaide showed that cells causing the rare genetic disorder cystic fibrosis could be… Continue Reading
Spotting Birds of a Feather
John Atkinson became a birder in fifth grader when his teacher told the students to put away their science books and follow her outside.… Continue Reading

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