December 6, 2019
Why Payers Lag Drug Developers and Regulators in Embracing Real-World Evidence
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November 22, 2019
Addressing the Barriers to Accessing Experimental Therapies
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November 19, 2019
Australia Commits $37.5 Million to Develop Treatments for Rare Disorders
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November 10, 2019
NICE Recommends GW Pharmaceuticals’ Epidyolex for Rare Epileptic Seizures
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October 9, 2019
When Did Super Become a Bad Thing?
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October 8, 2019
FDA Provides $4.1 Million for Two Natural History Studies
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September 24, 2019
Rare Disease Patients Get Nod in UN Declaration on Universal Health Coverage
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September 13, 2019
Vertex Reaches Access Agreement with Scottish Government for CF Drugs
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September 4, 2019
USCIS Pulls Back Plan to Deport Undocumented Patients Getting Life-Saving Treatments
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September 4, 2019
NICE Recommends Use of Gene Therapy for Rare Inherited Eye Disorder
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August 27, 2019
ARM Issues Statement of Principles on Genome Editing
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