3.30.2018 … Continue Reading
3.22.2018 Rare Daily Staff The U.K.’s Medicines & Healthcare products Regulatory Agency said it would allow patients with the rare genetic lipid… Continue Reading
3.2.2018 Nearly a year ago, more than 400 members of spinal muscular atrophy community along with industry, clinicians, and researchers convened a… Continue Reading
2.27.2018 Rare Daily Staff U.S. Food and Drug Administration Commissioner Scott Gottlieb in a blog entry today outlined several steps the agency is… Continue Reading
Gottlieb Calls for $400 Million in Expanded FDA Funding in Part to Stimulate Investment in Rare Diseases
2.13.2018 Rare Daily Staff U.S. Food and Drug Administration Commissioner Scott Gottlieb called for developing clinical trial networks to improve the… Continue Reading
2.6.2018 Rare Daily Staff The National Organization for Rare Disorders along with 37 patient and provider organizations in a letter to leaders of the… Continue Reading
1.31.2018 … Continue Reading
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