June 26, 2019
U.K. Charity Launches Medical Cannabis Pilot
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March 25, 2019
FDA Issues Draft Guidance on Natural History Studies for Rare Diseases
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March 20, 2019
Cure SMA and Parent Project Muscular Dystrophy Form Collaboration to Collect RWD
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March 13, 2019
A High School Student Unlocks A Rare Disease Mystery
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February 27, 2019
A Rare Disease Gets Rock Star Treatment
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February 25, 2019
Congenital Hyperinsulinism International to Award $70,000 Grant for Research
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February 22, 2019
Ionis CEO Stanley Crooke Discusses Success as a Platform Technology Company
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February 4, 2019
UK Grant Supports Diagnosis and Treatment of Rare Diseases
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January 30, 2019
Study Suggest Imaging Technology Could Measure Disease Severity in Friedreich Ataxia
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December 13, 2018
Gilbert Family Foundation Announces $12 Million Gene Therapy Initiative in NF1
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