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A total of 8 posts are filed under Innovation
Sarepta Therapeutics Enters Collaboration with Duke University to Develop Gene Editing to Treat DMD
Rare Daily Staff Sarepta Therapeutics said it signed a research collaboration agreement with Duke University that grants the company an… Continue Reading
Learning from Rare Diseases
Matt Wilsey has liked to make the case that one justification for investing in rare disease research is that through it, we can unlock an… Continue Reading
Gene Editing Technology in Mice Shows Promises as Approach for DMD
Rare Daily Staff Scientists at the University of California, Berkeley have developed a way to deliver gene-editing technology inside cells,… Continue Reading
Grace Science Foundation and Stanford University Create Biobank for Ultra-Rare NGLY1 Deficiency
Rare Daily Staff The Grace Science Foundation and a clinical research team from Stanford University have created an open source biobank of… Continue Reading
University Manufacturing Facility Sees Opportunity in Rare Disease Niche
Rare Daily Staff The University of Tennessee Health Sciences Center is near completion on its effort to convert a warehouse on the eastern… Continue Reading