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A total of 1958 posts are filed under Uncategorized
FDA Awards Rare Pediatric Disease Designation to Sancilio Pharmaceuticals’ Sickle Cell Disease Therapy
Rare Daily Staff The U.S. Food and Drug Administration awarded Rare Pediatric Disease Designation to Sancilio Pharmaceuticals for the… Continue Reading
NIH awards nearly $100 million for Autism Centers of Excellence
Rare Daily Staff The National Institutes of Health said it made nine awards of research grants totaling nearly $100 million over the next… Continue Reading
Precision for Medicine Acquires Rare Disease-Focused CRO
Rare Daily Staff Precision for Medicine Acquires Rare Disease-Focused CRO Precision for Medicine said it acquired Agility Clinical, a… Continue Reading
Doctor, CSO, and Father: Hunting for Answers for Fragile X Children
Dr. Michael Tranfaglia serves as Medical Director and Chief Scientific Officer of FRAXA, a nonprofit organization based in Newburyport,… Continue Reading
2017 Rare Artist Contest Now Accepting Entries – Submit Your Work Today!
The EveryLife Foundation for Rare Diseases is excited to announce that the ninth annual Rare Artist contest is now open for submissions.… Continue Reading
Emergency Room Chaos: 8 Relatable Moments You Know All Too Well
Many rare disease patients feel overwhelmed by the all-too-common emergency room visit that ends in misunderstanding.  In response to this… Continue Reading
Alex Undiagnosed: A Neurodegenerative Disease Goes Unnamed
It’s been ten long years and no one knows what’s wrong with Alex. He’s been gradually worsening due to a progressive neurodegenerative… Continue Reading