Achromatopsia 2

Search Trials
Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3
Status:
Active, not recruiting
Last Changed:
Jan 14, 2022
First Changed:
Sep 12, 2017
Disease(s):
Achromatopsia
Intervention(s):
either AAV - CNGB3 or AAV - CNGA3
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Sep 14, 2021
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGA3 Achromatopsia
Status:
Recruiting
Last Changed:
Apr 6, 2021
First Changed:
Oct 17, 2016
Disease(s):
Achromatopsia
Intervention(s):
AGTC-402

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