Achromatopsia 2

Search Trials
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGA3 Achromatopsia
Status:
Recruiting
Last Changed:
Jul 11, 2019
First Changed:
Oct 17, 2016
Disease(s):
Achromatopsia
Intervention(s):
AGTC-402
Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGB3 Achromatopsia
Status:
Recruiting
Last Changed:
Mar 20, 2019
First Changed:
Nov 9, 2015
Disease(s):
Achromatopsia
Intervention(s):
rAAV2tYF-PR1.7-hCNGB3

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