Achromatopsia

Search Trials
PBA Use for Treatment of ATF6-/- Patients
Status:
Not yet recruiting
Last Changed:
Sep 11, 2019
First Changed:
Aug 1, 2019
Disease(s):
ACHROMATOPSIA 7
Intervention(s):
PBA
Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3
Status:
Recruiting
Last Changed:
Sep 12, 2019
First Changed:
Sep 12, 2017
Disease(s):
Achromatopsia
Intervention(s):
either AAV - CNGB3 or AAV - CNGA3
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection

Connect. Empower. Inspire.