Acyl-CoA Oxidase Deficiency

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A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Status:
Recruiting
Last Changed:
Sep 26, 2018
First Changed:
Jun 23, 2014
Disease(s):
Mucopolysaccharidosis Disorders
Intervention(s):
Stem Cell TransplantationIMD Preparative RegimenOsteopetrosis Only Preparative RegimenOsteopetrosis Haploidentical Only Preparative RegimencALD SR-A (Standard-Risk, Regimen A)cALD SR-B (Standard-Risk, Regimen B)cALD HR-D (High-Risk, Regimen C)cALD HR-D (High-Risk, Regimen D)

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