Adenosine Deaminase Deficiency

Search Trials
Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA Gene
Status:
Completed
Last Changed:
Sep 20, 2021
First Changed:
May 13, 2013
Disease(s):
ADA-SCID
Intervention(s):
Infusion of autologous EFS-ADA LV CD34+ (OTL-101)busulfanPEG-ADA ERT
Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy
Status:
Enrolling by invitation
Last Changed:
Sep 28, 2021
First Changed:
Jul 13, 2021
Disease(s):
Severe Combined Immunodeficiency Due to ADA Deficiency
Intervention(s):
Retroviral Insertion Site Analysis
Retroviral Insertion Site Methodology Study
Status:
Withdrawn
Last Changed:
Jul 15, 2020
First Changed:
Oct 16, 2017
Disease(s):
Immune System Diseases
Intervention(s):
Strimvelis
The Role of Bacteria and Genetic Variations in Cystic Fibrosis
Status:
Completed
Last Changed:
Jun 29, 2021
First Changed:
Aug 7, 2002
Disease(s):
Psuedomas Infection
A Clinical Study to Enable Process Validation of Commercial Grade OTL-101
Status:
Terminated
Last Changed:
Nov 18, 2021
First Changed:
Oct 28, 2019
Disease(s):
Severe Combined Immunodeficiency Due to ADA Deficiency
Intervention(s):
OTL-101

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