Adrenomyeloneuropathy

Search Trials
Effect of Pioglitazone Administered to Patients With Adrenomyeloneuropathy
Status:
Completed
Last Changed:
Sep 10, 2019
First Changed:
Mar 6, 2019
Disease(s):
Adrenomyeloneuropathy
Intervention(s):
Pioglitazone
Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD)
Status:
Recruiting
Last Changed:
Aug 12, 2019
First Changed:
Feb 25, 2019
Disease(s):
Cerebral Adrenoleukodystrophy (CALD)
Intervention(s):
Genetic
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Minnesota Adrenoleukodystrophy Registry Study (MARS) and Biobank
Status:
Recruiting
Last Changed:
Jun 6, 2019
First Changed:
Dec 31, 2018
Disease(s):
ALD (Adrenoleukodystrophy)
Intervention(s):
Medical Record AbstractionBiospecimen Sample Collection

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