Aromatic L-Amino Acid Decarboxylase Deficiency

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A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
Status:
Recruiting
Last Changed:
Jan 31, 2022
First Changed:
Aug 2, 2016
Disease(s):
AADC Deficiency
Intervention(s):
AAV2-hAADC
Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency
Status:
Completed
Last Changed:
Apr 28, 2017
First Changed:
Mar 26, 2015
Disease(s):
Aromatic L-amino Acid Decarboxylase Deficiency

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