Canavan Disease

Search Trials
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Oral Glyceryl Triacetate (GTA) in Newborns With Canavan
Status:
Unknown status
Last Changed:
Jun 21, 2011
First Changed:
Jul 30, 2008
Disease(s):
Canavan Disease
Intervention(s):
GTA (Glyceryl triacetate)GTA glyceryl triacetate
Lithium and Acetate for Canavan Disease
Status:
Withdrawn
Last Changed:
Apr 21, 2015
First Changed:
Apr 14, 2008
Disease(s):
Canavan Disease
Intervention(s):
Lithium Gluconate (drug) Glyceryl Triacetate GTA (drug)
A Natural History Study of Canavan Disease
Status:
Recruiting
Last Changed:
Jun 20, 2018
First Changed:
Aug 1, 2016
Disease(s):
Canavan Disease

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