Diabetes mellitus AND insipidus with optic atrophy AND deafness

Search Trials
Efficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome
Status:
Not yet recruiting
Last Changed:
Jun 28, 2021
First Changed:
Jun 25, 2021
Disease(s):
Wolfram Syndrome
Intervention(s):
Depakine
I-Tracking Neurodegeneration in Early Wolfram Syndrome
Status:
Recruiting
Last Changed:
Jun 4, 2021
First Changed:
May 15, 2019
Disease(s):
Wolfram Syndrome
Monogenic Diabetes Misdiagnosed as Type 1
Status:
Recruiting
Last Changed:
Oct 15, 2019
First Changed:
Jun 17, 2019
Disease(s):
Diabetes Mellitus, Type 1
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Sep 14, 2021
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo

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