Diamond-Blackfan Anemia 6

Search Trials
Bone Marrow Transplant With Abatacept for Non-Malignant Diseases
Status:
Completed
Last Changed:
Dec 26, 2019
First Changed:
Aug 7, 2013
Disease(s):
Hurler Syndrome
Intervention(s):
Abatacept
T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
Status:
Recruiting
Last Changed:
May 6, 2022
First Changed:
Aug 31, 2018
Disease(s):
Sickle Cell Anemia
Intervention(s):
CD3/CD19 depleted leukocytesCD45RA depleted leukocytesHydroxyureaRituximabAlemtuzumabFludarabineThiotepa
The Use of Trifluoperazine in Transfusion Dependent DBA
Status:
Terminated
Last Changed:
Oct 20, 2021
First Changed:
May 29, 2019
Disease(s):
Diamond Blackfan Anemia
Intervention(s):
Trifluoperazine
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Dec 21, 2021
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo

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