Gaucher disease type 2

Search Trials
Lentiviral Vector Gene Therapy – The Guard1 Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Status:
Recruiting
Last Changed:
Dec 29, 2021
First Changed:
Oct 30, 2019
Disease(s):
Gaucher Disease
Intervention(s):
AVR-RD-02
Lentiviral Vector Gene Therapy – The GuardOne Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Status:
Recruiting
Last Changed:
Sep 2, 2021
First Changed:
Oct 30, 2019
Disease(s):
Gaucher Disease
Intervention(s):
AVR-RD-02
Phase 1/2 Lentiviral Vector Gene Therapy – The GuardOne Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Status:
Recruiting
Last Changed:
Feb 17, 2020
First Changed:
Oct 30, 2019
Disease(s):
Gaucher Disease
Intervention(s):
AVR-RD-02
In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases
Status:
Recruiting
Last Changed:
Apr 9, 2021
First Changed:
Aug 31, 2020
Disease(s):
MPS I
Intervention(s):
Aldurazyme (laronidase)
Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)
Status:
Recruiting
Last Changed:
Sep 23, 2021
First Changed:
Jun 2, 2020
Disease(s):
Gaucher Disease, Type 2
Intervention(s):
PR001MethylprednisoloneSirolimusPrednisone

Connect. Empower. Inspire.