Glycogen Storage Disease

Search Trials
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14
Status:
Recruiting
Last Changed:
Jan 25, 2019
First Changed:
Jan 19, 2018
Disease(s):
Glycogen Storage Disease, Type 14
Intervention(s):
ORL-1G - D-galactose
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
Respiratory Muscle Training in L-Onset Pompe Disease (LOPD)
Status:
Recruiting
Last Changed:
May 1, 2018
First Changed:
Jun 16, 2016
Disease(s):
Glycogen Storage Disease Type II
Intervention(s):
RMT therapy using modified RMT deviceSham-RMT therapy using modified RMT device

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