Hemoglobin H Disease

Search Trials
Multicentric Prospective Study to Screen Inborn Errors of Metabolism in Non-immune Hydrops (NIH) Fetalis by Massively Parallel Sequencing
Status:
Recruiting
Last Changed:
Oct 14, 2021
First Changed:
Mar 16, 2020
Disease(s):
Non-Immune Hydrops Fetalis
Intervention(s):
NON-IMMUNE HYDROPS FETALIS diagnosis
Whole Exome Sequencing and Whole Genome Sequencing for Non-immune Fetal/Neonatal Hydrops
Status:
Recruiting
Last Changed:
Jun 29, 2021
First Changed:
Apr 11, 2019
Disease(s):
Non-immune Fetal Hydrops
Intervention(s):
Whole Exome SequencingWhole Genome Sequencing
Collection of Human Biospecimens for Basic and Clinical Research Into Alpha Globin Variants
Status:
Recruiting
Last Changed:
Sep 14, 2021
First Changed:
May 6, 2019
Disease(s):
Alpha Thalassemia
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Status:
Recruiting
Last Changed:
Oct 15, 2021
First Changed:
Feb 25, 2021
Disease(s):
Transfusion-dependent Alpha-Thalassemia
Intervention(s):
Placebo Matching MitapivatMitapivat
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)
Status:
Not yet recruiting
Last Changed:
Jul 13, 2021
First Changed:
Feb 25, 2021
Disease(s):
Non-Transfusion-dependent Alpha-Thalassemia
Intervention(s):
Placebo Matching MitapivatMitapivat

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