Leber congenital amaurosis

Search Trials
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
A Patient Registry Study for Patients Treated With Voretigene Neparvovec
Status:
Recruiting
Last Changed:
Dec 17, 2018
First Changed:
Jul 24, 2018
Disease(s):
Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
Intervention(s):
AAV2-hRPE65v2,voretigene neparvovec-rzyl
Safety Study of RPE65 Gene Therapy to Treat Leber Congenital Amaurosis
Status:
Completed
Last Changed:
Dec 7, 2015
First Changed:
Mar 26, 2008
Disease(s):
Retinal Degeneration
Intervention(s):
tgAAG76 (rAAV 2/2.hRPE65p.hRPE65)

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