Pompe disease

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Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)
Status:
Not yet recruiting
Last Changed:
Dec 20, 2021
First Changed:
Dec 20, 2021
Disease(s):
Glycogen Storage Disease Type II
Intervention(s):
Avalglucosidase alfa (GZ402666)
Frequency of Pompe Disease in Patients With Myalgia With or Without Hyper Ckemia – Data From the Reference Center (CERCA)
Status:
Recruiting
Last Changed:
Oct 29, 2021
First Changed:
Oct 25, 2021
Disease(s):
Pompe Disease
MSOT in Pompe Disease
Status:
Not yet recruiting
Last Changed:
Oct 19, 2021
First Changed:
Oct 19, 2021
Disease(s):
Pompe Disease
Intervention(s):
Multispectral Optoacoustic Tomography
Higher Dose of Alglucosidase Alpha for Pompe Disease
Status:
Not yet recruiting
Last Changed:
Aug 23, 2021
First Changed:
Aug 23, 2021
Disease(s):
Glycogen Storage Disease Type II
Intervention(s):
Alglucosidase Alfa

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