Pompe disease

Search Trials
Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (ATBIG-Pompe-Study)
Status:
Enrolling by invitation
Last Changed:
Feb 20, 2018
First Changed:
Jul 6, 2016
Disease(s):
Pompe Disease
Intervention(s):
glucosidase alfa
AAV2/8-LSPhGAA in Late-Onset Pompe Disease
Status:
Recruiting
Last Changed:
Jan 30, 2019
First Changed:
May 23, 2018
Disease(s):
Pompe Disease
Intervention(s):
AAV2/8LSPhGAA
Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease
Status:
Recruiting
Last Changed:
Jan 24, 2019
First Changed:
Sep 15, 2014
Disease(s):
Pompe Disease
Intervention(s):
Recombinant Adeno-Associated Virus Acid Alpha-GlucosidaseRapamycinsalineRituxanDiphenhydramineAcetaminophenLidocaineLMX 4 Topical Cream
A Long Term Follow up Study in Late-onset Pompe Disease
Status:
Unknown status
Last Changed:
Dec 4, 2013
First Changed:
Jul 11, 2008
Disease(s):
Pompe Disease
Pompe Disease QMUS and EIM
Status:
Active, not recruiting
Last Changed:
Apr 10, 2018
First Changed:
Apr 19, 2016
Disease(s):
Pompe Disease
Intervention(s):
Muscle ultrasoundElectrical Impedance Myography

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