Pompe disease

Search Trials
Albuterol in Individuals With Late Onset Pompe Disease (LOPD)
Status:
Completed
Last Changed:
Feb 12, 2016
First Changed:
May 22, 2013
Disease(s):
Pompe Disease
Intervention(s):
Albuterol
Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease
Status:
Completed
Last Changed:
Feb 6, 2018
First Changed:
Jun 25, 2013
Disease(s):
Pompe Disease
Intervention(s):
AlbuterolPlacebo
VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Participants With Late-Onset Pompe Disease
Status:
Active, not recruiting
Last Changed:
Jan 29, 2019
First Changed:
Sep 13, 2016
Disease(s):
Pompe Disease
Intervention(s):
VAL-1221RhGAA
A Natural History Study of Adult Onset Pompe Disease Using Muscle MRI
Status:
Unknown status
Last Changed:
Aug 30, 2013
First Changed:
Aug 2, 2013
Disease(s):
Pompe Disease
A Pilot Study of Pyridostigmine in Pompe Disease
Status:
Terminated
Last Changed:
May 15, 2018
First Changed:
Feb 6, 2015
Disease(s):
Pompe Disease
Intervention(s):
Pyridostigmine Bromide

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