Shwachman syndrome

Search Trials
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Status:
Recruiting
Last Changed:
Aug 7, 2019
First Changed:
Apr 5, 2019
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
Status:
Withdrawn
Last Changed:
Mar 18, 2019
First Changed:
Nov 27, 2017
Disease(s):
Progressive Familial Intrahepatic Cholestasis (PFIC)
Intervention(s):
MaralixibatPlacebo
Second-line Therapy of Unresectable Cholangiocarcinoma by RADIOEMBOLIZATION
Status:
Terminated
Last Changed:
Aug 7, 2013
First Changed:
Jun 28, 2011
Disease(s):
Cholestasis, Progressive Familial Intrahepatic 3
Intervention(s):
Yttrium microsphere injection
CD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell Transplant
Status:
Recruiting
Last Changed:
Mar 13, 2019
First Changed:
Feb 13, 2014
Disease(s):
Chronic Myeloid Leukemia (CML)
Intervention(s):
CliniMACS CD34+ Reagent SystemThiotepaCyclophosphamideAlemtuzumabTacrolimusMelphalanBusulfanFludarabineMethylprednisolone
Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases
Status:
Active, not recruiting
Last Changed:
Jan 29, 2019
First Changed:
Sep 4, 2014
Disease(s):
Primary Immune Deficiency Disorders
Intervention(s):
BPX-501 and AP1903

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