Hanson Wade

As investment in gene therapies continues to grow rapidly, more effectively engaging patients throughout development has become a priority for any company serious about building safer and more meaningful gene therapy programs.

In this context, the 2nd Annual Gene Therapy Patient Engagement Summit will unite patient advocacy and engagement leaders from gene therapy and gene editing drug developers, patient groups and patients themselves to address the specific challenges of genetic therapy patient engagement, generating actionable insights through detailed case studies and open, honest discussions.

Join us to hear directly from companies and institutions including Spark Therapeutics, Ultragenyx, FDA, Global Genes, and CRISPR Therapeutics on key topics including managing expectations across gene therapy development, navigating patient input on one-time transformative treatments with novel clinical trial designs combined with extensive follow-ups, and developing educational materials on gene therapy to raise awareness in collaboration with patient advocacy organizations. Leverage their knowledge and experiences to ultimately ensure effective creation and implementation of patient-centric gene therapy programs.

From: 06/07/2022 - To: 06/09/2022

All day event

1 Avenue De Lafayette, Boston, Massachusetts, United States of America

Featured Speakers

Alison Bateman-House
Assistant Professor, Department of Population Health
NYU
Amy Fisher
Head of Patient Advocacy
Spark Therapeutics
Anne Rowzee
Associate Director for Policy, CBER
FDA
Annie Ganot
Founder & VP Patient Advocacy
Solid Biosciences
Craig Martin
CEO
Global Genes
Edgar Vega
Senior Manager, Patient Advocacy
uniQure
Fernanda Copeland
Global Head, Patient Advocacy & Engagement
AVROBIO
Halley Losekamp
Director, Patient Enrolment
AGTC
Jennifer Helfer
Head, Patient Advocacy & Engagement
Encoded Therapeutics
Jodi Wolff
VP, Patient Engagement & Advocacy
StrideBio
Jordanna Mora
Senior Director, Patient Advocacy & Centricity
Beam Therapeutics
Karen Jackler
Program Manager, Patient Engagement, CBER
FDA
Kate Trenam
Head of Patient Engagement, Early Research
UCB
Kristen Bostrom
Associate Director, Global Patient Advocacy & Engagement
BioMarin
Kristin Voorhees
Director, Patient Advocacy
Ultragenyx
Pat Furlong
Founding President & CEO Parent Project Muscular Dystrophy
Parent Project Muscular Dystrophy
Paula Orandash
Patient Engagement Liaison, Community Education Gene Therapy
PTC Therapeutics
PJ Brooks
Deputy Director, Officer of Rare Diseases Research
NIH
Safiyya Gassman
Senior Director, Policy & Public Affairs
Pfizer
Sara Davis
Senior Director, Patient Advocacy & Government Affairs
CRISPR Therapeutics
Sarah Friedhoff
Associate Director, Patient Advocacy & Clinical Affairs
Abeona Therapeutics
Tom Croce
VP, Patient Advocacy
bluebird bio
Vivian Fernandez
Senior Director, Patient Advocacy
REGENXBIO
Wendy Borsari
Senior Manager, Patient Advocacy
Tenaya Therapeutics
X