Are Oligonucleotide Therapeutics Right for Your Disease?

Are you wondering if RNAi (RNA interference) or antisense oligonucleotide (ASO) therapeutics are right for your rare disease? Hear from experts on recent developments in oligonucleotide therapeutics for rare diseases and understand what conditions and mutations are a best fit. You will also learn about recent developments in N-of-1 ASO and customized therapeutics and develop strategies to de-risk early therapeutic development and analyze common roadblocks.

In this discussion you will learn about:
– Oligonucleotide therapeutics and how they work
– The types of rare diseases that are best suited to oligonucleotide therapeutics
– Considerations before pursuing this option

Meet your featured speakers for this session:

• Sanath Kuman Ramesh
• Rodney Samaco
• Kristina Bowyer
• Daniel O’Reilly