Ways to Engage

Join the Portal

Take the next step to connect with the rare disease community. Create a profile to connect with others, read resources and post to the event hub.

Share Your Story

It’s our experiences that shapes you and inspires others. Share your rare story with us.

Events

RARE Patient Advocacy Summit
From: 09/27/2021 To: 09/29/2021
All day event
Virtual Event:
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Resources

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News

July 28, 2021
Deep Genomics Raises $180 Million to Advance Programmable RNA Therapeutics
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July 28, 2021
Aristea Enters into Collaboration with Arena in Neutrophil-Mediated Diseases and Raises $63 Million
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July 28, 2021
Ring Raises $117 Million to Advance Vector Platform to Unlock Full Potential of Gene Therapy
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July 28, 2021
Bluebird Bio Forms Strategic Alliance with Resilience to Develop Next Generation Cell Therapies
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July 28, 2021
FDA Grants Fast Track Designation to Apic Bio’s APB-102 for the Treatment of Patients with SOD1 ALS
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July 28, 2021
FDA Grants Rare Pediatric Disease Designation to Lexeo Therapeutics CLN2 Batten Disease Therapy
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