RARECast: Gene Therapies Bring New Hope to Rare Disease Patients

One of the most promising areas for rare disease treatments is gene therapy, part of the emerging area of regenerative medicine. We spoke to Karen Kozarsky, Managing Partner at Vector Partners, prior to the Alliance for Regenerative Medicine’s January 27 round table on rare diseases. Kozarsky discussed the promise gene therapy holds for rare diseases, the challenges in developing these therapies, and the progress being made.

RARECast is a weekly series by Daniel S. Levine. Levine is an award-winning business journalist who has reported on the life sciences, economic development, and business policy issues throughout his 25-year career. He founded Levine Media Group in 2013, which produces The Bio Report and RARECast podcasts. Read his full bio here.