GalXC Quest: Dicerna Bets on Its Unqiue Approach to RNAi


A range of RNAi therapies are moving through clinical development and toward the market providing the promise of new ways to treat genetic diseases. Dicerna, which has a platform that allows for a unique delivery mechanism for targeting the liver with RNAi therapies, recently began dosing patients in an early-stage trial of its experimental RNAi therapy to treat hyperoxaluria, a rare genetic liver disease. We spoke to Doug Fambrough, president and CEO of Dicerna, about the company’s GalXC platform, what makes it unique, and what’s ahead in its pipeline.

 
 

Filed Under: Business, Drug Development, Global Genes, RARECast Podcasts

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