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Rare Daily Staff A National Institutes of Health team has identified a compound already approved by the […]
Read moreEvotec and Bristol Myers Squibb Extend and Expand Strategic Neurodegeneration Partnership
Rare Daily Staff Evotec said it has extended and expanded its strategic neurodegeneration partnership with Bristol Myers […]
Read moreBPGbio Expands Partnership with debra of America for Epidermolysis Bullosa Phase 2/3 Trial
Rare Daily Staff AI-powered biopharma BPGbio has reached a partnership agreement with debra for America for BPGbio’s […]
Read moreResilience Approved for $410 Million Loan from the Department of Defense to Establish Resilient Biomanufacturing Capacity
Rare Daily Staff National Resilience, a biomanufacturing company dedicated to broadening access to complex medicines, said it […]
Read moreGamida Cell Cuts Workforce, Discontinues Programs as it Awaits Potential FDA Approval
Rare Daily Staff Gamida Cell revealed a strategic restructuring to prioritize the potential approval and launch of […]
Read moreBlind Chef Uses Visibility to Advocate for Rare Disease
Christine Ha taught herself to cook while in college. As a finance student at the University of […]
Read moreFDA Issues Says It Won’t Approve Incyte’s Ruxolitinib Extended Release Tablets to Treat Rare Blood Disorders
Rare Daily Staff The U.S. Food and Drug Administration has issued to Incyte a complete response letter […]
Read moreAddressing the Barriers to Patient Participation in Clinical Trials
A significant obstacle to getting patients to participate in rare disease clinical trials, particularly children, is the […]
Read moreGovernment of Canada Improves Access to Affordable and Effective Drugs for Rare Diseases
Rare Daily Staff The Canadian government said it would invest $1.1 billion (CAN$1.5 billion) over three years […]
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