Spotting Birds of a Feather

John Atkinson became a birder in fifth grader when…

FDA Grants Rare Pediatric Disease Designation to Prometic’s Experimental Alsotröm Syndrome Drug
Rare Daily Staff The U.S. Food and Drug Administration has granted Prometic Life Sciences a Rare Pediatric Disease designation for its small… Continue Reading
Mallinckrodt Forms Rare Disease Research Partnership with Washington University
Rare Daily Staff Specialty pharmaceutical company Mallinckrodt said it have formed a rare disease research partnership with Washington… Continue Reading
CureGenetics raises $17 million
Rare Daily Staff China-based CureGenetics said it closed a $17 million series A financing, which will be used to optimize its gene editing… Continue Reading
Partnership Formed to Develop Gene Therapy for Cystic Fibrosis
Rare Daily Staff Oxford BioMedica said it has entered into a process development collaboration agreement with the UK Cystic Fibrosis Gene… Continue Reading
Ovid Reports Mixed Results from Angelman Syndrome Study
Rare Daily Staff Ovid Therapeutics said topline data from a mid-stage trial showed its experimental therapy OV101 for the rare condition… Continue Reading
Akcea and PTC Collaborate to Commercialize Rare Disease Drugs in Latin America
Rare Daily Staff PTC Therapeutics and Akcea Therapeutics said they will collaborate to commercialize two of Akcea’s rare disease drugs… Continue Reading
Rare Leader: Taylor Gurganus, Chair and Co-Founder, Bohring-Opitz Syndrome Foundation
The Basics Name: Taylor Gurganus Title: Chair and co-founder Organization: Bohring-Opitz Syndrome Foundation Disease focus: Bohring-Opitz… Continue Reading

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