September 14, 2019
A Randomized Controlled Trial of Eculizumab in AQP4 Antibody-positive Participants With NMO (PREVENT Study)
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September 14, 2019
Biomarker for Niemann Pick Type C Disease (BioNPC)
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September 14, 2019
Phenotypes, Biomarkers and Pathophysiology in Hereditary Spastic Paraplegias and Related Disorders
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September 14, 2019
Biomarker for Hereditary Angioedema Disease Type 1 (BioHAE)
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September 14, 2019
Biomarker for Hurler Disease (BioHurler)
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September 14, 2019
Biomarker for Morquio Disease (BioMorquio)
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September 14, 2019
A Study to Explore the Long-Term Safety and Efficacy of TEV-48125 (Fremanezumab) for the Prevention of Cluster Headache
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January 30, 2019
Biomarker for Wolman Disease: BioWolman
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January 30, 2019
Biomarker for Hyaline Fibromatosis Syndrome
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January 30, 2019
Biomarker for Krabbe Disease: BioKrabbe
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January 30, 2019
European Alpha-Mannosidosis Patient Epidemiological Program
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January 30, 2019
Biomarker for Sanfilippo Type A-B-C-D Disease Sanfilippo Type A-B-C-D [MPS III]
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