Tag: BioMarin

A total of 17 posts are filed under BioMarin
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Global Genes to Host Fourth Annual Tribute to Champions of Hope Gala and Patient Advocacy Summit
On September 26th, 2015, over 650 attendees from across the globe will gather at the Hyatt Regency Resort and Spa in Huntington Beach, CA,… Continue Reading
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CureDuchenne Celebrates Submission of First-Ever New Drug Application for Duchenne Muscular Dystrophy
CureDuchenne Celebrates Submission of First-Ever New Drug Application for Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping;… Continue Reading
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Exclusivity: How The Government Keeps Orphan Drugs in Production
Why did the FDA grant BioMarin this permission, known in bureaucratic lingo as a “six-month pediatric exclusivity extension?” BioMarin… Continue Reading
Biomarin
BioMarin Gets U.S. Panel’s Backing on Rare Disease Drug
BioMarin Pharmaceutical Inc. received the backing of U.S. advisers for a drug to treat a rare metabolic disease that can affect growth. The… Continue Reading
Roche CEO Severin Schwan
Is Roche Going to Do Some Big Rare Disease Drug Deals?
So is Roche going to do some rare disease deals or not? Rumors of a possible buyout of Alexion and BioMarin– alternatively dissed and… Continue Reading
Ultragenyx
Startup Ultragenyx Snags PiII Program for Growing Rare-Disease Pipeline
Flush from raising more than $100 million, Novato, CA-based startup Ultragenyx Pharmaceutical has stepped up with a new pact to partner on… Continue Reading
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Nimbus Discovery, Shire to Co-Develop Oral Rare Disease Drugs
Nimbus Discovery splashed onto the scene in 2011 with a big-name investor group that included Bill Gates and a plan to discover drugs with… Continue Reading