Tag: cyclodextrin

A total of 9 posts are filed under cyclodextrin
Hayley Fights Niemann Pick Type C Using Compassionate Use Program and Cyclodextrin
Hayley was diagnosed with Niemann Pick Type C (NPC) in October of 2011. However, she had been living with the symptoms since she was six-… Continue Reading
Science Magazine: Rare Diseases and Rare Opportunities
On 24 October 2014, after a daylong meeting to plan a rare disease clinical trial, Raymond Wang hopped into a cab and pulled out his… Continue Reading
WSJ Reports: Small Biotech Gets Rights to Rare Disease Drug
The National Institutes of Health licensed rights to cyclodextrin to a biotechnology company that will take on development of the drug for… Continue Reading
Top Hospitals and Doctors Fail To Find Elevated Bilirubin Levels and Enlarged Spleen at Birth as Niemann Pick Type C disease
Chase was born on August 21, 2009, in Jacksonville Florida. He arrived a bit early via C-Section. At two days old, his bilirubin levels were… Continue Reading
WSJ Health Blog Reports – Results in Mice May Help Shape Clinical Trial for Children With Rare Fatal Disease
By Amy Dockser Marcus, Wall Street Journal Health Blog It’s a well-known maxim in science that curing a disease in a rodent doesn’t… Continue Reading
PARENT DRIVEN RESEARCH – Innovations from the trenches!
A Push to spur more drugs for deadly rare diseases LAURAN NEERGAARD, AP Medical Writer Cassidy Hempel, 6, waves at hospital staff with the… Continue Reading
Children’s Hospital Oakland Receives FDA Clearance to Begin World’s First Cyclodextrin Administration Into the Brains of Twins with Rare and Deadly Cholesterol Disease
Sugar Molecule Used in Common Food and Household Products Like Febreze® Fabric Refresher Called Hydroxypropyl Beta Cyclodextrin (HPßCD)… Continue Reading