Tag: FDA

A total of 130 posts are filed under FDA
FDA Grants Priority Review Status to Ultragenyx
Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE), a biopharmaceutical company focused on the development of novel products for rare and… Continue Reading
NYT: Senate Confirms Scott Gottlieb to Head F.D.A.
The Senate voted 57 to 42 on Tuesday to confirm Dr. Scott Gottlieb as commissioner of the Food and Drug Administration, where he will be… Continue Reading
Horizon Pharma plc Announces FDA Approval to Expand the Age Range for RAVICTI® to People with Urea Cycle Disorders Ages Two Months +
Horizon Pharma plc (NASDAQ:HZNP), a biopharmaceutical company focused on improving patients’ lives by identifying, developing, acquiring… Continue Reading
Scott Gottlieb Nomination Approved
Global Genes joined the rare community to support Dr. Scott Gottlieb’s nomination to serve as Commissioner of Food and Drug… Continue Reading
BioPharma Dive: 5 Trends Shaping Rare Disease Drug Development
Story by Ned Pagliarulo Amid ongoing scrutiny of rising prescription drug costs, a three decade-old law has become a new flash point in the… Continue Reading
Designing Effective Rare Disease Registries
by Raymond A. Huml, MS, DVM, RAC and Margaret Dean, MBA, Quintiles MS at DDDmag.com   Rare disease research was once a neglected aspect of… Continue Reading
Teva Announces FDA Approval of AUSTEDO™ (deutetrabenazine) Tablets for the Treatment of Chorea Associated with Huntington’s Disease
Teva Pharmaceutical Industries Ltd. (NYSE and TASE: TEVA) today announced that the U.S. Food and Drug Administration (FDA) has approved… Continue Reading
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