January 7, 2016
Rare Disease Report: FDA Approves Alexion’s Kanuma for LAL Deficiency
Read More
June 20, 2015
Rare Disease Report: National Lipid Association (NLA) Scientific Sessions 2015
Read More
October 29, 2014
Synageva Biopharma Makes New Moves with Sebelipase Alfa for LAL Deficiency
Read More
March 1, 2013
Synageva BioPharma Joins NORD, Eurordis and Global Genes Project in Support of Rare Disease Day 2013
Read More
August 6, 2012
Darling Dakota’s Life Taken By Rare Lysosomal Storage Disorder Called Wolman’s Disease
Read More
X